Cystic fibrosis affects the lungs, but delivering gene therapy to the defective cells is difficult.
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CRISPR gene editing therapy has the potential to overcome major challenges that have hindered previous gene therapies and provide an effective, long-term treatment for cystic fibrosis.
The technique successfully edited the DNA of hard-to-reach lung stem cells in mice, and the changes persisted for at least 22 months — essentially the entire life of the animals, the researchers said. Daniel Siegward At the University of Texas Southwestern Medical Center.
“I nearly fell off my chair in amazement when I saw that the effects were sustained for several months,” he said. “This is exciting news for the potential treatment of a variety of lung diseases.”
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Source: www.newscientist.com
